
Matteo’s first day of school
Hear an SMA family describe the moment their son walked into class on the first day of school and why it means so much to them.
Navigating life with SMA
Navigating life with SMA
MILAN: Caregivers need to be knowledgeable about SMA because it’s going to affect the way the child grows up.
ELENA: We need to always look for things that might come up and how, how can we help these kids the best way possible. So when they grow up, it will make a big difference for their life.
TINA: We’re always looking at new therapies to see what we can do to help with Malachi gain strength. We’re going along and learning things as he grows. There’s a lot of information out there, so sometimes you just have to take a step back and kind of go and look at it at your own pace.
MATT: We’re learning now to help us prepare for the future. I think some of the advice I would say is don’t lose sight of what’s important. And not in a cliché way, but in a very real way. There’s a lot of little things that therapists tell you to do in between appointments. Take the little things seriously.
LAURA: Getting treatment for SMA is kind of like step one. And then your whole life is ahead of you. So you want to make sure that your child has everything they need to grow and thrive.
TINA: This is a life that none of us anticipated. It’s nothing that we ever expected. But you will do what you need to for your child at the end of the day. You won’t let them give up, so you don’t give up.
Close the transcriptHear an SMA family describe the moment their son walked into class on the first day of school and why it means so much to them.
Even though a child receives treatment for his or her SMA, it doesn’t mean their care stops. Hear from SMA caregivers about how they learned to be strong advocates for their children in the years following treatment.
Learn how newborn screening and having SMA treatments can help improve the lives of children with SMA.
Hear from SMA families
What is the most important information I should know about
ZOLGENSMA?
What is the most important information I should know about ZOLGENSMA?
What should I watch for before and after infusion with ZOLGENSMA?
What do I need to know about vaccinations and ZOLGENSMA?
Do I need to take precautions with the patient’s bodily waste?
What are the possible or likely side effects of ZOLGENSMA?
What is ZOLGENSMA?
ZOLGENSMA is a prescription gene therapy used to treat children less than 2 years old with spinal muscular atrophy (SMA). ZOLGENSMA is given as a one-time infusion into a vein. ZOLGENSMA was not evaluated in patients with advanced SMA.
The safety information provided here is not comprehensive. Talk to the patient’s doctor about any side effects that bother the patient or that don’t go away.
You are encouraged to report suspected side effects by contacting the FDA at 1-800-FDA-1088 or www.fda.gov/medwatch, or Novartis Gene Therapies, Inc. at 833-828-3947.
Please see the Full Prescribing Information.