
Helpful resources
Aniya has 4 copies of SMN2 gene
Treated at 5 months old
Before receiving treatment with ZOLGENSMA,
Aniya received another SMA treatment.
Whether you are just exploring your treatment options or have finished treatment with ZOLGENSMA® (onasemnogene abeparvovec-xioi), the resources below can help wherever your family is in their spinal muscular atrophy (SMA) journey.
Treatment Resources

Prenatal SMA Diagnosis Checklist
If you receive a prenatal diagnosis, learn what you can do to prepare for your child to get treatment as soon as possible.
- About SMA and gene replacement therapy
- Connecting with a support team
- Additional lab tests to prepare for
- Contacting your insurance provider to ask about plan options

Doctor Discussion Guide
A helpful resource for preparing to talk to your child’s doctor about your treatment goals:
- What you need to know about SMA
- How ZOLGENSMA can help
- Questions to ask your child’s doctor
- Safety considerations

Steps to Treating With ZOLGENSMA Brochure
Step-by-step instructions with a checklist, starting from the first day of your ZOLGENSMA prescription to after infusion day:
- Initial tests and screening
- Connecting with Novartis Patient SupportTM for guidance and support
- Insurance process
- Treatment day
- Posttreatment support

Post-Appointment Flashcard
A flashcard featuring the steps you should plan to take following your child's treatment with ZOLGENSMA.
- Reminders about what to expect after treatment
- Posttreatment testing information
- Posttreatment guidance on monitoring
- Follow-up appointment calendar

A Caregiver's Guide to ZOLGENSMA
A comprehensive guide about ZOLGENSMA and SMA including:
- Facts about SMA
- How ZOLGENSMA works
- Clinical trials
- Safety
- Treatment with ZOLGENSMA
Need help finding a treatment center?
You can reach out to Cure SMA ↗ or the Muscular Dystrophy Association (MDA) ↗.
SMA & Gene Replacement Therapy

Explaining SMA & ZOLGENSMA to Others
How to talk to others about your child’s treatment—and a diagnosis they most likely haven’t heard of:
- Facts about SMA
- How ZOLGENSMA can help
- SMA after treatment

SMA After Treatment
Your medical care team is there to help support you and your child throughout your journey. In addition to your doctor, your team might include a lung specialist (pulmonologist) and a physical therapist.
Learn about medical care team members and other support for children with SMA with the Preparing for SMA After Treatment PDF.