
Lucy’s sister shows the way
For Lucy, who was diagnosed with SMA through newborn screening, having a supportive sibling has made for many fun memorable moments. Watch how these sisters work together to get Lucy up and walking with assistance.
Navigating life with SMA
Navigating life with SMA
STEPHANIE: Ryker just turned 2 years old, and this is such a huge milestone for us and for SMA kids because without treatment, Type 1 kids are only given until 2 years old to live.
STEPHANIE: The reason that it’s so memorable for us is because my daughter Aizlynn was born in 2012 and there were no treatments for SMA.
GLEN: Ryker and Aizlynn, they both have 2 totally different stories. And through the pain and the heartache, we’ve found the ability to find grace, beauty, love, all sorts of amazing things that we just would have never ever experienced. The hope and the new possibilities that are there is just incredibly exciting.
STEPHANIE: My hopes for Ryker’s future are that he continues to develop the way that he is. I would love to see him be able to walk without assistance. One of my biggest hopes is just to be able to see him grow up and graduate high school and get married—and those were things that we didn’t get to see our daughter do.
GLEN: But you don’t know what’s gonna happen tomorrow. So take it a day at a time and just love, you know, those children, the absolute best that you can and let them experience life the best way that they can.
Close the transcriptFor Lucy, who was diagnosed with SMA through newborn screening, having a supportive sibling has made for many fun memorable moments. Watch how these sisters work together to get Lucy up and walking with assistance.
Watch the first time Brady, who was diagnosed with SMA Type 2, pulled himself to stand independently in his walker.
Check out resources and advice from other caregivers to help you navigate your child’s future with SMA.
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What is the most important information I should know about
ZOLGENSMA?
What is the most important information I should know about ZOLGENSMA?
What should I watch for before and after infusion with ZOLGENSMA?
What do I need to know about vaccinations and ZOLGENSMA?
Do I need to take precautions with the patient’s bodily waste?
What are the possible or likely side effects of ZOLGENSMA?
What is ZOLGENSMA?
ZOLGENSMA is a prescription gene therapy used to treat children less than 2 years old with spinal muscular atrophy (SMA). ZOLGENSMA is given as a one-time infusion into a vein. ZOLGENSMA was not evaluated in patients with advanced SMA.
The safety information provided here is not comprehensive. Talk to the patient’s doctor about any side effects that bother the patient or that don’t go away.
You are encouraged to report suspected side effects by contacting the FDA at 1-800-FDA-1088 or www.fda.gov/medwatch, or Novartis Gene Therapies, Inc. at 833-828-3947.
Please see the Full Prescribing Information.