
Preparing for the future
Hear the perspectives of multiple families about why it’s important to be knowledgeable about SMA and its management even after treatment.
Navigating life with SMA
Navigating life with SMA
CIJI:
One of my most memorable moments was, we were driving home from Utah and Maisie was in the back.
And she just started going, “Ma-Ma-Ma.”
I wasn’t sure if I was ever gonna hear that.
Without treatment, SMA [Type 1] robs their abilities to smile, to talk, to ever lift their head, to ever speak.
I couldn’t pull over immediately because I was driving on I-70 and I was like, “I gotta find a spot baby, but I hear you, I hear you.”
I pulled over and I just held her and loved her and was like, “Yay, you said ‘Momma.’”
Then when I tried to get back in the car to drive, she was like, “Ma-Ma-Ma-Ma.” And then it was like, “Hey, Maisie, I need to drive.” But the whole trip home was Ma-Ma-Ma.
It was pretty awesome.
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Hear an SMA family describe the moment their son walked into class on the first day of school and why it means so much to them.
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What is the most important information I should know about
ZOLGENSMA?
What is the most important information I should know about ZOLGENSMA?
What should I watch for before and after infusion with ZOLGENSMA?
What do I need to know about vaccinations and ZOLGENSMA?
Do I need to take precautions with the patient’s bodily waste?
What are the possible or likely side effects of ZOLGENSMA?
What is ZOLGENSMA?
ZOLGENSMA is a prescription gene therapy used to treat children less than 2 years old with spinal muscular atrophy (SMA). ZOLGENSMA is given as a one-time infusion into a vein. ZOLGENSMA was not evaluated in patients with advanced SMA.
The safety information provided here is not comprehensive. Talk to the patient’s doctor about any side effects that bother the patient or that don’t go away.
You are encouraged to report suspected side effects by contacting the FDA at 1-800-FDA-1088 or www.fda.gov/medwatch, or Novartis Gene Therapies, Inc. at 833-828-3947.
Please see the Full Prescribing Information.