
Brady goes mobile
Watch the first time Brady, who was diagnosed with SMA Type 2, pulled himself to stand independently in his walker.
Navigating life with SMA
Navigating life with SMA
STEVE: A recent milestone for Lucy was when she started walking with assistance. Her sister recently actually grabbed her by both hands and started walking backwards in a way that I thought would be a little too fast, but Lucy was actually able to keep pace with her into the other room.
STEVE: It was significant because it was that interaction with her sister that we were looking for and hoping for ever since she was born.
ASHLEY: With the natural progression of SMA, we didn’t know if these moments would ever actually happen. I didn’t know if I would ever see the day, you know, that Noralynn was taking her hands and walking across the floor or watching them play together with blocks. Or, you know, even just climbing up on the couch together and sliding back down. And here we are today that I watch it, you know, on a daily basis with the two of them.
STEVE: Seeing how Noralynn loves her little sister and how Lucy looks up to her big sister, it’s very meaningful and special and it’s what we were hoping to see.
Close the transcriptWatch the first time Brady, who was diagnosed with SMA Type 2, pulled himself to stand independently in his walker.
Achieving a new milestone in SMA is always cause for celebration. Hear Joe and Annie recount the moment their daughter, Quinn, received her leg braces and was able to stand for the first time.
Check out resources and advice from other caregivers to help you navigate your child’s future with SMA.
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What is the most important information I should know about
ZOLGENSMA?
What is the most important information I should know about ZOLGENSMA?
What should I watch for before and after infusion with ZOLGENSMA?
What do I need to know about vaccinations and ZOLGENSMA?
Do I need to take precautions with the patient’s bodily waste?
What are the possible or likely side effects of ZOLGENSMA?
What is ZOLGENSMA?
ZOLGENSMA is a prescription gene therapy used to treat children less than 2 years old with spinal muscular atrophy (SMA). ZOLGENSMA is given as a one-time infusion into a vein. ZOLGENSMA was not evaluated in patients with advanced SMA.
The safety information provided here is not comprehensive. Talk to the patient’s doctor about any side effects that bother the patient or that don’t go away.
You are encouraged to report suspected side effects by contacting the FDA at 1-800-FDA-1088 or www.fda.gov/medwatch, or Novartis Gene Therapies, Inc. at 833-828-3947.
Please see the Full Prescribing Information.