
Quinn proudly stands
Achieving a new milestone in SMA is always cause for celebration. Hear Joe and Annie recount the moment their daughter, Quinn, received her leg braces and was able to stand for the first time.
Navigating life with SMA
Navigating life with SMA
NICOLE: A memorable time was when Brady pulled to stand independently on his walker. In true Brady style, Brady pulled up to his walker without any assistance when no one was expecting it. He did it and he stared at us like we were crazy, like he’d been doing it forever.
TYLER: That was something we had been working on for months and months for him to be strong enough to stand up in his walker and walk across the house on his own. That was such a huge milestone, something that we had wanted from the very beginning.
NICOLE: Being able to get into his walker on his own and to take off where he wants to go, was, it opened up Brady’s world. He can now get to the ball if he wants it or go to the sandbox if he wants to. And it’s also opened our world up, where we have to chase him more, but we’ll take it.
NICOLE: He just does it like it’s no big deal now. Like he’s been doing it forever and he’s surprised that we’re excited every time now. He rolls his eyes and goes on about his way.
Close the transcriptAchieving a new milestone in SMA is always cause for celebration. Hear Joe and Annie recount the moment their daughter, Quinn, received her leg braces and was able to stand for the first time.
Hear about Olivia as she gets her first wheelchair, discovers her world, and explores some of her newfound independence in this video.
Check out resources and advice from other caregivers to help you navigate your child’s future with SMA.
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What is the most important information I should know about
ZOLGENSMA?
What is the most important information I should know about ZOLGENSMA?
What should I watch for before and after infusion with ZOLGENSMA?
What do I need to know about vaccinations and ZOLGENSMA?
Do I need to take precautions with the patient’s bodily waste?
What are the possible or likely side effects of ZOLGENSMA?
What is ZOLGENSMA?
ZOLGENSMA is a prescription gene therapy used to treat children less than 2 years old with spinal muscular atrophy (SMA). ZOLGENSMA is given as a one-time infusion into a vein. ZOLGENSMA was not evaluated in patients with advanced SMA.
The safety information provided here is not comprehensive. Talk to the patient’s doctor about any side effects that bother the patient or that don’t go away.
You are encouraged to report suspected side effects by contacting the FDA at 1-800-FDA-1088 or www.fda.gov/medwatch, or Novartis Gene Therapies, Inc. at 833-828-3947.
Please see the Full Prescribing Information.