
Preparing for the future
Hear the perspectives of multiple families about why it’s important to be knowledgeable about SMA and its management even after treatment.
Navigating life with SMA after treatment
Navigating life with SMA after treatment
CIJI:
One of my most memorable moments was, we were driving home from Utah and Maisie was in the back.
And she just started going, “Ma-Ma-Ma.”
I wasn’t sure if I was ever gonna hear that.
Without treatment, SMA [Type 1] robs their abilities to smile, to talk, to ever lift their head, to ever speak.
I couldn’t pull over immediately because I was driving on I-70 and I was like, “I gotta find a spot baby, but I hear you, I hear you.”
I pulled over and I just held her and loved her and was like, “Yay, you said ‘Momma.’”
Then when I tried to get back in the car to drive, she was like, “Ma-Ma-Ma-Ma.” And then it was like, “Hey, Maisie, I need to drive.” But the whole trip home was Ma-Ma-Ma.
It was pretty awesome.
Close the transcriptHear the perspectives of multiple families about why it’s important to be knowledgeable about SMA and its management even after treatment.
The first day of preschool was just one of the many monumental firsts for Matteo. Watch this video to see his family’s excitement and hear how much school means to them.
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What is the most important information I should know about
ZOLGENSMA?
What is the most important information I should know about
ZOLGENSMA?
What should I watch for before and after infusion with
ZOLGENSMA?
What do I need to know about vaccinations and ZOLGENSMA?
Do I need to take precautions with the patient’s bodily waste?
What are the possible or likely side effects of ZOLGENSMA?
What is ZOLGENSMA?
ZOLGENSMA is a prescription gene therapy used to treat children less than 2 years
old with spinal muscular atrophy (SMA). ZOLGENSMA is given as a one-time infusion
into a vein. ZOLGENSMA was not evaluated in patients with advanced SMA.
The safety information provided here is not comprehensive. Talk to the patient’s doctor about any side effects that bother the patient or that don’t go away.
You are encouraged to report suspected side effects by contacting the FDA at 1-800-FDA-1088 or www.fda.gov/medwatch, or AveXis at 833-828-3947.
Please see the Full Prescribing Information.